Pharmaceutical Articles – Medicines For The Treatment Of Rare Diseases In The Republic Of For 2025. 1,N07xx06,Tetrabenazine,25Mg,Tablet,Tablet,2,M01cc01,Penicillamine,250Mg,Tablet/Capsule,Tablet/Capsule,3,A16ax05,Zinc Acetate,50Mg,Capsule,Hard,Capsule,4,N07xx08,Tafamidis,20Mg,Capsule,Soft,Capsule,5,N07xx02,Riluzole,50Mg,Film-Coated Tablet,Tablet,6, A16ax06, Miglustat, 100Mg, Capsule, Hard, Capsule,7,A16ab12,Elosulfase Alfa,5Mg/5Ml,Concentrate For Solution For Infusion,Vial,8,A16ab09,Idursulfase,6Mg/3Ml,Concentrate For Solution For Infusion,Vial,9,L04ac07,Tocilizumab,200Mg/10Ml,Concentrate For Solution For Infusion,Ampoule,10,A16ab02,Imiglucerase,400Ie,Powder For Concentrate For Solution For Infusion,Vial,11,B06ac01,Human C1- Esterase Inhibitor,500Ie,Powder And Vehicle For Solution For Injection Or Infusion,Powder Vial + Solvent Vial + Administration Set,12,G04be03,Sildenafil,20Mg,Film-Coated Tablet,Tablet,13,A16ax07,Sapropterin,100Mg,Tablet For Oral Solution,Tablet,14,C02da01,Diazoxide,25Mg,Capsule/Hard Tablet,Capsule/Hard Tablet,15,H05aa02,Teriparatide,20 Mcg/80 Mcl,Solution For Injection,Pre-Filled Pen,16,N03ag04,Vigabatrin,500Mg,Film-Coated Tablet/Tablet For Oral Solution,Tablet,17,L01xe10,Everolimus,2.5Mg,Tablet/Dispersible Tablet,Tablet,18,A16ax04,Nitisinone,5 Mg,Capsule,Hard,Capsule,19,N03ax17,Stiripentol,250Mg,Hard Capsule/Powder For Oral Suspension,Hard Capsule/Powder For Oral Suspension,20,G04be03,Sildenafil,50 Mg,Film-Coated Tablet/Tablet,Tablet,21,C02kx01,Bosentan,125Mg,Film-Coated Tablet,Tablet,22,L01xe18,Ruxolitinib,5Mg,Tablet,Tablet,23,B06ac04,Conestat Alfa,2100Ie,Powder For Solution For Injection,Vial,24,V03ac03,Deferasirox,360Mg,Film-Coated Tablet,Tablet,25,A16ab11,Taliglucerase Alfa,200Ie,Powder For Solution For Infusion,Vial,26,B02bx05,Eltrombopag,50Mg,Tablet,Tablet,27,B02bd07,Coagulation Factor Xiii,250 Iu,Powder And Vehicle For Solution For Injection Or Infusion,Powder And Vehicle For Solution For Injection Or Infusion,28,L04aa10,Sirolimus,1Mg,Coated Tablet,Tablet,29,L04ax05,Pirfenidone,267Mg,Film-Coated Tablet/Capsule,Tablet/Capsule,30,A16ax10,Eliglustat,84Mg,Capsule,Hard,Capsule,31,M09ax07,Nusinersen,12Mg/5Ml,Solution For Injection,Vial,32,B01ac21,Treprostinil,5Mg/Ml,Solution For Infusion (Subcutaneous And Intravenous Use),Vial,33,A16ab10,Velaglucerase Alfa,400Ie,Powder For Solution For Infusion,Vial,34,B06ac02,Icatibant,30Mg/3 Ml,Solution For Injection,Pre-Filled Syringe,35,A16ax12,Trientine,200Mg,Capsule,Hard,Capsule,36,L01ex09,Nintedanib,150Mg,Capsule,Soft,Capsule,37,M09ax10,Risdiplam,0.75Mg/Ml,Powder For Oral Suspension,Bottle,38,J06ba01,Immunoglobulins, Normal Human,200Mg/Ml,Solution For Injection,Vial X 5Ml,39,J06ba01,Immunoglobulins, Normal Human,200Mg/Ml,Solution For Injection,Vial X 20Ml,40,B06ac01,Human C1-Esterase Inhibitor (Subcutaneous Form),2000Ie,Powder And Solvent For Subcutaneous Application,Vial With Powder + Vial With Solvent + Set For Subcutaneous Application,41,R07ax02,Ivacaftor,150Mg,Film-Coated Tablet,Tablet,42,В06ав01,Human Hemin,250Mg/10Ml,Concentrate For Solution For Infusion,Ampoule,43,L04ac03,Anakinra,100Mg/0.67Ml (150Mg/Ml),Solution For Injection,1 Pre-Filled Syringe X 0.67Ml,44,H01cb05,Pasireotide,40Mg,Powder And Solvent For Suspension For Injection,Vial,45,N07xx08,Tafamidis,61Mg,Capsule,Soft,Capsule,46,A16ax18,Lumasiran,94.5Mg/0.5 Ml,Solution For Injection,Vial,47,G04bx16,Tiopronin,300Mg,Delayed-Release Tablet,Tablet,48,G04bx16,Tiopronin,100Mg,Delayed-Release Tablet,Tablet,49,M05bx07,
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